Home Pediatrics Pediatrics Research Programs Center for Gene Therapy Posters & Publications Close Pediatrics Research Department of Research Back to Center for Gene Therapy Meet Our Team Posters & Publications Gene Therapy Research Research Bonkowsky Lab UPIN Communications Search Publications ASGCT 2025 AAV Mini-Dystrophin Gene Therapy for Duchenne Muscular Dystrophy: a Phase 1b Trial ASGCT 2024 Beacon of Hope - Gold Award for Excellence from AAMC Conference Posters 2025 Implementation of an Institutional Gene Therapy Safety Committee at the University of Utah AAV Delivery of ADAR Mediated RNA Editing for Treatment of Collagen VI-Related Muscular Dystrophy Bonkowsky Lab - AAV-Mediated Gene Supplementation in Combination with Microglial Replacement for Vanishing White Matter Disease Using Circulation-Derived Myeloid Cells (CDMCs)
